There are many challenges in finding an effective, long-lasting and universal cure for the whole cohort of patients with Duchenne muscular dystrophy (DMD). The discovery of H19 lncRNA as a stabiliser of dystrophin may prove to be the missing link to the success of various rescue therapies proposed for treating DMD.

中文翻译：

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H19 lncRNA 拯救肌营养不良蛋白

在为整个杜氏肌营养不良症 (DMD) 患者群体寻找有效、持久和普遍的治疗方法方面存在许多挑战。H19 lncRNA 作为抗肌萎缩蛋白稳定剂的发现可能被证明是为治疗 DMD 提出的各种挽救疗法成功的缺失环节。