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Base editing-mediated splicing correction therapy for spinal muscular atrophy.
Cell Research ( IF 28.1 ) Pub Date : 2020-03-24 , DOI: 10.1038/s41422-020-0304-y Xiang Lin 1, 2 , Haizhu Chen 1 , Ying-Qian Lu 1 , Shunyan Hong 1 , Xinde Hu 3 , Yanxia Gao 3 , Lu-Lu Lai 1 , Jin-Jing Li 1 , Zishuai Wang 4 , Wenqin Ying 3 , Lixiang Ma 5 , Ning Wang 1, 2 , Erwei Zuo 4 , Hui Yang 3 , Wan-Jin Chen 1, 2
中文翻译:
基础编辑介导的脊柱肌萎缩症的剪接校正疗法。
更新日期:2020-03-24
Cell Research ( IF 28.1 ) Pub Date : 2020-03-24 , DOI: 10.1038/s41422-020-0304-y Xiang Lin 1, 2 , Haizhu Chen 1 , Ying-Qian Lu 1 , Shunyan Hong 1 , Xinde Hu 3 , Yanxia Gao 3 , Lu-Lu Lai 1 , Jin-Jing Li 1 , Zishuai Wang 4 , Wenqin Ying 3 , Lixiang Ma 5 , Ning Wang 1, 2 , Erwei Zuo 4 , Hui Yang 3 , Wan-Jin Chen 1, 2
Affiliation
中文翻译:
基础编辑介导的脊柱肌萎缩症的剪接校正疗法。