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Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic
Cell ( IF 64.5 ) Pub Date : 2024-03-14 , DOI: 10.1016/j.cell.2024.02.015
Todd Logan , Matthew J. Simon , Anil Rana , Gerald M. Cherf , Ankita Srivastava , Sonnet S. Davis , Ray Lieh Yoon Low , Chi-Lu Chiu , Meng Fang , Fen Huang , Akhil Bhalla , Ceyda Llapashtica , Rachel Prorok , Michelle E. Pizzo , Meredith E.K. Calvert , Elizabeth W. Sun , Jennifer Hsiao-Nakamoto , Yashas Rajendra , Katrina W. Lexa , Devendra B. Srivastava , Bettina van Lengerich , Junhua Wang , Yaneth Robles-Colmenares , Do Jin Kim , Joseph Duque , Melina Lenser , Timothy K. Earr , Hoang Nguyen , Roni Chau , Buyankhishig Tsogtbaatar , Ritesh Ravi , Lukas L. Skuja , Hilda Solanoy , Howard J. Rosen , Bradley F. Boeve , Adam L. Boxer , Hilary W. Heuer , Mark S. Dennis , Mihalis S. Kariolis , Kathryn M. Monroe , Laralynne Przybyla , Pascal E. Sanchez , Rene Meisner , Dolores Diaz , Kirk R. Henne , Ryan J. Watts , Anastasia G. Henry , Kannan Gunasekaran , Giuseppe Astarita , Jung H. Suh , Joseph W. Lewcock , Sarah L. DeVos , Gilbert Di Paolo



中文翻译:

用脑渗透性颗粒体蛋白前体生物制剂拯救由 Grn 功能丧失引起的溶酶体贮积症

更新日期:2024-03-14
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