Molecular Therapy - Methods & Clinical Development
Volume 17, 12 June 2020, Pages 429-440
Original ArticleThe mRNA-Binding Protein IGF2BP1 Restores Fetal Hemoglobin in Cultured Erythroid Cells from Patients with β-Hemoglobin Disorders
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open access
Graphical Abstract
Keywords
fetal hemoglobin
beta-thalassemia
sickle cell disease
lentivirus
IGF2BP1
hemoglobinopathies
gene therapy
gene regulation
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© 2020 The Author(s).