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Corrigendum to "The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII" [Mol Genet Metab 2020 Mar;129(3):219-227].
Molecular Genetics and Metabolism ( IF 3.8 ) Pub Date : 2020-08-22 , DOI: 10.1016/j.ymgme.2020.08.001
Raymond Y Wang 1 , José Francisco da Silva Franco 2 , Jaime López-Valdez 3 , Esmeralda Martins 4 , Vernon Reid Sutton 5 , Chester B Whitley 6 , Lin Zhang 7 , Tricia Cimms 7 , Deborah Marsden 7 , Agnieszka Jurecka 7 , Paul Harmatz 8
Affiliation  



中文翻译:

更正“在患有粘多糖贮积症VII的受试者中施用法诺酮酶α,rhGUS酶替代疗法的长期安全性和有效性” [Mol Genet Metab 2020 Mar; 129(3):219-227]。

更新日期:2020-08-22
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