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Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria.
The New England Journal of Medicine ( IF 158.5 ) Pub Date : 2020-06-11 , DOI: 10.1056/nejmoa1913147 Manisha Balwani 1 , Eliane Sardh 1 , Paolo Ventura 1 , Paula Aguilera Peiró 1 , David C. Rees 1 , Ulrich Stölzel 1 , D. Montgomery Bissell 1 , Herbert L. Bonkovsky 1 , Jerzy Windyga 1 , Karl E. Anderson 1 , Charles Parker 1 , Samuel M. Silver 1 , Siobán B. Keel 1 , Jiaan-Der Wang 1 , Penelope E. Stein 1 , Pauline Harper 1 , Daphne Vassiliou 1 , Bruce Wang 1 , John Phillips 1 , Aneta Ivanova 1 , Janneke G. Langendonk 1 , Raili Kauppinen 1 , Elisabeth Minder 1 , Yutaka Horie 1 , Craig Penz 1 , Jihong Chen 1 , Shangbin Liu 1 , John J. Ko 1 , Marianne T. Sweetser 1 , Pushkal Garg 1 , Akshay Vaishnaw 1 , Jae B. Kim 1 , Amy R. Simon 1 , Laurent Gouya 1
The New England Journal of Medicine ( IF 158.5 ) Pub Date : 2020-06-11 , DOI: 10.1056/nejmoa1913147 Manisha Balwani 1 , Eliane Sardh 1 , Paolo Ventura 1 , Paula Aguilera Peiró 1 , David C. Rees 1 , Ulrich Stölzel 1 , D. Montgomery Bissell 1 , Herbert L. Bonkovsky 1 , Jerzy Windyga 1 , Karl E. Anderson 1 , Charles Parker 1 , Samuel M. Silver 1 , Siobán B. Keel 1 , Jiaan-Der Wang 1 , Penelope E. Stein 1 , Pauline Harper 1 , Daphne Vassiliou 1 , Bruce Wang 1 , John Phillips 1 , Aneta Ivanova 1 , Janneke G. Langendonk 1 , Raili Kauppinen 1 , Elisabeth Minder 1 , Yutaka Horie 1 , Craig Penz 1 , Jihong Chen 1 , Shangbin Liu 1 , John J. Ko 1 , Marianne T. Sweetser 1 , Pushkal Garg 1 , Akshay Vaishnaw 1 , Jae B. Kim 1 , Amy R. Simon 1 , Laurent Gouya 1
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New England Journal of Medicine, Volume 382, Issue 24, Page 2289-2301, June 2020.
中文翻译:
RNAi治疗Givosiran治疗急性间歇性卟啉症的3期试验。
2020年6月,《新英格兰医学杂志》第382卷第24期,第2289-2301页。
更新日期:2020-06-11
中文翻译:
RNAi治疗Givosiran治疗急性间歇性卟啉症的3期试验。
2020年6月,《新英格兰医学杂志》第382卷第24期,第2289-2301页。